Authors: Kasun Kodippili, Chady H. Hakim, Matthew J. Burke, Yongping Yue, James A. Teixeira, Keqing Zhang, Gang Yao, Gopal J. Babu, Roland W. Herzog, Dongsheng Duan

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 2, Pp 101268- (2024)

Subject Terms: Duchenne muscular dystrophy, DMD, SERCA2a, AAV, canine model, muscle function, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000846; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/8999a19b16ac45ccb94ac3fd43620ab2

Authors: Junping Zhang, Xiangping Yu, Matthew Chrzanowski, Jiahe Tian, Derek Pouchnik, Ping Guo, Roland W. Herzog, Weidong Xiao

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101215- (2024)

Subject Terms: adeno-associated virus, AAV, TMCA-AAVseq, noncanonical AAV genomes, molecular configuration, library construction, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000317; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/237c8bb4f21e4619a8750ef8f842ece1

Authors: Jyoti Rana, Roland W. Herzog, Maite Muñoz-Melero, Kentaro Yamada, Sandeep R.P. Kumar, Anh K. Lam, David M. Markusic, Dongsheng Duan, Cox Terhorst, Barry J. Byrne, Manuela Corti, Moanaro Biswas

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101216- (2024)

Subject Terms: gene therapy, AAV, immune suppression, redosing, re-administration, capsid, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000329; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/dbfee83096ee41878357669ddf1b4522

Authors: Junping Zhang, Dylan A. Frabutt, Matthew Chrzanowski, Ning Li, Lohra M. Miller, Jiahe Tian, Patrick L. Mulcrone, Anh K. Lam, Benjamin E. Draper, Martin F. Jarrold, Roland W. Herzog, Weidong Xiao

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101206- (2024)

Subject Terms: Adeno-associated virus, self-complementary AAV vectors, covalently closed-end double-stranded AAV, transduction, genome integrity, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000226; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/ba0fb73ec32b4ab08090643c484cf170

Authors: Xin Li, Lohra Mickelle Miller, Matthew Chrzanowski, Jiahe Tian, Martin F. Jarrold, Roland W. Herzog, Weidong Xiao, Benjamin Draper, Junping Zhang

Superior Title: Frontiers in Bioengineering and Biotechnology, Vol 11 (2023)

Subject Terms: adeno-associated virus, invert terminal repeat, small genome, packaging signal, replicative intermediates, Biotechnology, TP248.13-248.65

File Description: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fbioe.2023.1327433/full; https://doaj.org/toc/2296-4185

Access URL: https://doaj.org/article/b644a5a27ba2402b86be15f164c43ac0

Authors: Moanaro Biswas, Kaman So, Thais B. Bertolini, Preethi Krishnan, Jyoti Rana, Maite Muñoz-Melero, Farooq Syed, Sandeep R. P. Kumar, Hongyu Gao, Xiaoling Xuei, Cox Terhorst, Henry Daniell, Sha Cao, Roland W. Herzog

Superior Title: Frontiers in Immunology, Vol 14 (2023)

Subject Terms: FoxP3+ regulatory T cells, latency associated peptide (LAP), oral tolerance, antidrug antibodies (ADA), single cell RNA and transcriptome sequencing, Immunologic diseases. Allergy, RC581-607

File Description: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fimmu.2023.1278184/full; https://doaj.org/toc/1664-3224

Access URL: https://doaj.org/article/305eae01744641ecb9a275cdec627bbe

Authors: Yuanbojiao Zuo, Chen Zhang, Yuan Zhou, Haiwen Li, Weidong Xiao, Roland W. Herzog, Jie Xu, Jifeng Zhang, Y. Eugene Chen, Renzhi Han

Superior Title: Cell & Bioscience, Vol 13, Iss 1, Pp 1-9 (2023)

Subject Terms: ANGPTL3, Cholesterol, Base editing, Base editor, Cardiovascular disease, CVD, Biotechnology, TP248.13-248.65, Biology (General), QH301-705.5, Biochemistry, QD415-436

File Description: electronic resource

Relation: https://doaj.org/toc/2045-3701

Access URL: https://doaj.org/article/01189687d1df469ca9f410bb5526ff84

Authors: Patrick L. Mulcrone, Anh K. Lam, Dylan Frabutt, Junping Zhang, Matthew Chrzanowski, Roland W. Herzog, Weidong Xiao

Superior Title: Scientific Reports, Vol 13, Iss 1, Pp 1-14 (2023)

Subject Terms: Medicine, Science

File Description: electronic resource

Relation: https://doaj.org/toc/2045-2322

Access URL: https://doaj.org/article/3995dcbcc1cb483fa7902a0c60257d86

Authors: Patrick L. Mulcrone, Roland W. Herzog, Weidong Xiao

Superior Title: Molecular Therapy: Oncolytics, Vol 27, Iss , Pp 73-88 (2022)

Subject Terms: gene therapy, rAAV, cancer, tumor microenvironment, tissue tropism, AAV design, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2372770522001218; https://doaj.org/toc/2372-7705

Access URL: https://doaj.org/article/00736ddb79e44d51ad347054e804a84b

Authors: Anh K. Lam, Junping Zhang, Dylan Frabutt, Patrick L. Mulcrone, Lei Li, Lifan Zeng, Roland W. Herzog, Weidong Xiao

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 185-194 (2022)

Subject Terms: AAV, capsid characterization, LC-MS, peptide mapping, engineered capsids, gene therapy, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050122001334; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/19ab892021054159a919044b17f3e279

Authors: Junping Zhang, Ping Guo, Xiangping Yu, Dylan A. Frabutt, Anh K. Lam, Patrick L. Mulcrone, Matthew Chrzanowski, Jenni Firrman, Derek Pouchnik, Nianli Sang, Yong Diao, Roland W. Herzog, Weidong Xiao

Superior Title: Molecular Therapy: Nucleic Acids, Vol 29, Iss , Pp 852-861 (2022)

Subject Terms: MT: Oligonucleotides, Therapies and Applications, recombinant adeno-associated virus (rAAV) vectors, subgenomic particles, DNA lesion/break, non-homologous end joining, Therapeutics. Pharmacology, RM1-950

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2162253122002268; https://doaj.org/toc/2162-2531

Access URL: https://doaj.org/article/c6c9ec66ff5f44fb9ea07ac49a6b0bc3

Authors: Sandeep R.P. Kumar, Jun Xie, Shilang Hu, Jihye Ko, Qifeng Huang, Harrison C. Brown, Alok Srivastava, David M. Markusic, Christopher B. Doering, H. Trent Spencer, Arun Srivastava, Guangping Gao, Roland W. Herzog

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 23, Iss , Pp 98-107 (2021)

Subject Terms: adeno-associated virus, AAV, hemophilia, factor IX, liver, non-human primate, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050121001273; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/c8c0531282d4473082e53448b9e6d260

Authors: Chady H. Hakim, Sandeep R. P. Kumar, Dennis O. Pérez-López, Nalinda B. Wasala, Dong Zhang, Yongping Yue, James Teixeira, Xiufang Pan, Keqing Zhang, Emily D. Million, Christopher E. Nelson, Samantha Metzger, Jin Han, Jacqueline A. Louderman, Florian Schmidt, Feng Feng, Dirk Grimm, Bruce F. Smith, Gang Yao, N. Nora Yang, Charles A. Gersbach, Shi-jie Chen, Roland W. Herzog, Dongsheng Duan

Superior Title: Nature Communications, Vol 12, Iss 1, Pp 1-12 (2021)

Subject Terms: Science

File Description: electronic resource

Relation: https://doaj.org/toc/2041-1723

Access URL: https://doaj.org/article/fa789cec57864e868cf64db8cae359c5

Authors: Moanaro Biswas, Damien Marsic, Ning Li, Chenhui Zou, Gloria Gonzalez-Aseguinolaza, Irene Zolotukhin, Sandeep R.P. Kumar, Jyoti Rana, John S.S. Butterfield, Oleksandr Kondratov, Ype P. de Jong, Roland W. Herzog, Sergei Zolotukhin

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 19, Iss , Pp 347-361 (2020)

Subject Terms: AAV3, gene therapy, hepatocyte, directed evolution, seroprevalence, neutralizing antibody, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050120302047; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/05f6a412488548bf8d9ee4437f4100f3

Authors: Chenhui Zou, Koen O.A. Vercauteren, Eleftherios Michailidis, Mohammad Kabbani, Irene Zoluthkin, Corrine Quirk, Luis Chiriboga, Mustafa Yazicioglu, Xavier M. Anguela, Philip Meuleman, Katherine A. High, Roland W. Herzog, Ype P. de Jong

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 18, Iss , Pp 189-198 (2020)

Subject Terms: humanized mice, AAV, gene therapy, liver, human hepatocytes, donor variability, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050120301200; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/76e8a94fb75547cf982881d7ea650537

Authors: Thais B. Bertolini, Jamie L. Shirley, Irene Zolotukhin, Xin Li, Tsuneyasu Kaisho, Weidong Xiao, Sandeep R. P. Kumar, Roland W. Herzog

Superior Title: Frontiers in Immunology, Vol 12 (2021)

Subject Terms: CD8+ T cell, dendritic cells, CpG, adeno-associated virus, TLR9, gene therapy, Immunologic diseases. Allergy, RC581-607

File Description: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fimmu.2021.672449/full; https://doaj.org/toc/1664-3224

Access URL: https://doaj.org/article/2a3a6ab4719142409e8c223560c4bfa4

Authors: Sandeep R. P. Kumar, Xiaomei Wang, Nagavardhini Avuthu, Thais B. Bertolini, Cox Terhorst, Chittibabu Guda, Henry Daniell, Roland W. Herzog

Superior Title: Frontiers in Immunology, Vol 11 (2020)

Subject Terms: hemophilia, oral tolerance, transgenic plant, regulatory T (Treg) cell, factor IX, Immunologic diseases. Allergy, RC581-607

File Description: electronic resource

Relation: https://www.frontiersin.org/article/10.3389/fimmu.2020.00844/full; https://doaj.org/toc/1664-3224

Access URL: https://doaj.org/article/958639e910c34829881cb10a9057ce09

Authors: Brett Palaschak, Damien Marsic, Roland W. Herzog, Sergei Zolotukhin, David M. Markusic

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 5, Iss C, Pp 142-152 (2017)

Subject Terms: AAV vector, capsid immunity, mouse model, hemophilia, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050117300591; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/8cb46ba869564c8980d91cf54bc5ee63

Authors: Xiaomei Wang, Roland W. Herzog, Barry J. Byrne, Sandeep R.P. Kumar, Qi Zhou, Christian J. Buchholz, Moanaro Biswas

Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 5, Iss C, Pp 76-82 (2017)

Subject Terms: hemophilia B, CD20, SCFV, lentivirus, gene transfer, measles virus, psuedotype, Genetics, QH426-470, Cytology, QH573-671

File Description: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050117300505; https://doaj.org/toc/2329-0501

Access URL: https://doaj.org/article/cbfc10cca4284189aca738ec77b936ec

Authors: David M. Markusic, Timothy C. Nichols, Elizabeth P. Merricks, Brett Palaschak, Irene Zolotukhin, Damien Marsic, Sergei Zolotukhin, Arun Srivastava, Roland W. Herzog

Superior Title: Journal of Translational Medicine, Vol 15, Iss 1, Pp 1-11 (2017)

Subject Terms: AAV, Gene therapy, Hemophilia B, Factor IX, Capsid, Medicine

File Description: electronic resource

Relation: http://link.springer.com/article/10.1186/s12967-017-1200-1; https://doaj.org/toc/1479-5876

Access URL: https://doaj.org/article/f621a02988f943ae9689ad35be3ac336