Authors: Moanaro Biswas, Damien Marsic, Ning Li, Chenhui Zou, Gloria Gonzalez-Aseguinolaza, Irene Zolotukhin, Sandeep R.P. Kumar, Jyoti Rana, John S.S. Butterfield, Oleksandr Kondratov, Ype P. de Jong, Roland W. Herzog, Sergei Zolotukhin
Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 19, Iss , Pp 347-361 (2020)
Subject Terms: AAV3, gene therapy, hepatocyte, directed evolution, seroprevalence, neutralizing antibody, Genetics, QH426-470, Cytology, QH573-671
File Description: electronic resource
Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 5, Iss C, Pp 142-152 (2017)
Subject Terms: AAV vector, capsid immunity, mouse model, hemophilia, Genetics, QH426-470, Cytology, QH573-671
File Description: electronic resource
Authors: David M. Markusic, Timothy C. Nichols, Elizabeth P. Merricks, Brett Palaschak, Irene Zolotukhin, Damien Marsic, Sergei Zolotukhin, Arun Srivastava, Roland W. Herzog
Superior Title: Journal of Translational Medicine, Vol 15, Iss 1, Pp 1-11 (2017)
Subject Terms: AAV, Gene therapy, Hemophilia B, Factor IX, Capsid, Medicine
File Description: electronic resource
Authors: Damien Marsic, Héctor R Méndez-Gómez, Sergei Zolotukhin
Superior Title: Molecular Therapy: Methods & Clinical Development, Vol 2, Iss , Pp - (2015)
File Description: electronic resource
Authors: Damien Marsic, A L Byrne-steele, Joseph D Ng
Contributors: The Pennsylvania State University CiteSeerX Archives
Superior Title: http://www.biomedcentral.com/content/pdf/1472-6750-8-44.pdf.
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Authors: Elena V. Pikuta, Damien Marsic, Takashi Itoh, Asim K. Bej, Jane Tang, William B. Whitman, Joseph D. Ng, Owen K. Garriott, Richard B. Hoover
Contributors: The Pennsylvania State University CiteSeerX Archives
Superior Title: http://ijsb.sgmjournals.org/content/57/7/1612.full.pdf.
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Relation: http://citeseerx.ist.psu.edu/viewdoc/summary?doi=10.1.1.322.9439; http://ijsb.sgmjournals.org/content/57/7/1612.full.pdf
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Authors: Richard B. Hoover, Elena V. Pikuta, Asim K. Bej, Damien Marsic, William B. Whitman, Jane Tang, Paul Krader
Contributors: The Pennsylvania State University CiteSeerX Archives
Superior Title: http://ijs.sgmjournals.org/content/53/3/815.full.pdf.
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Relation: http://citeseerx.ist.psu.edu/viewdoc/summary?doi=10.1.1.322.7417; http://ijs.sgmjournals.org/content/53/3/815.full.pdf
Availability: http://ijs.sgmjournals.org/content/53/3/815.full.pdf